GSNOR overexpression enhances CAR-T stemness and anti-tumor function by enforcing mitochondrial fitness.

in Molecular therapy : the journal of the American Society of Gene Therapy by Qing Niu, Haixiao Zhang, Fang Wang, Xing Xu, Yuechen Luo, Baolin He, Mingxia Shi, Erlie Jiang, Xiaoming Feng

TLDR

  • The study looked at how a type of treatment called CAR-T therapy works for people with certain types of cancer. The treatment involves taking cells from the patient's body, genetically modifying them to recognize and attack cancer cells, and then putting the modified cells back into the patient's body. However, not everyone who gets this treatment responds well to it. The study found that a chemical called nitric oxide (NO) can make the modified cells less effective at attacking cancer cells. The study also found that adding a protein called S-nitrosoglutathione reductase (GSNOR) to the modified cells can help them better attack cancer cells and be more effective at the treatment. The study suggests that this protein could be used to improve CAR-T therapy outcomes for people with certain types of cancer.

Abstract

Chimeric antigen receptor T cell (CAR-T) has been developed as a promising agent for patients with refractory or relapsed lymphoma and leukemia, but not all the recipients could achieve a long-lasting remission. The limited capacity of in vivo expansion and memory differentiation post activation is one of the major reasons for suboptimal CAR-T therapeutic efficiency. Nitric oxide (NO) plays multifaceted roles in mitochondrial dynamics and T-cell activation, but its function on CAR-T cell persistence and anti-tumor efficacy remains unknown. Herein, we found the continuous signaling from CAR not only promotes excessive NO production, but also suppressed S-nitrosoglutathione reductase (GSNOR) expression in T cells, which collectively led to increased protein S-nitrosylation, resulting in impaired mitochondrial fitness and deficiency of T cell stemness. Intriguingly, enforced expression of GSNOR promoted memory differentiation of CAR-T cell after immune activation, rendered CAR-T better resistance to mitochondrial dysfunction, further enhanced CAR-T cell expansion and anti-tumor capacity in vitro and in mouse tumor model. Thus, we revealed a critical role of NO in restricting CAR-T cell persistence and functionality, and defined that GSNOR overexpression may provide a solution to combat NO stress and render patients with more durable protection from CAR-T therapy.

Overview

  • The study investigates the role of nitric oxide (NO) in chimeric antigen receptor T cell (CAR-T) therapy for refractory or relapsed lymphoma and leukemia patients. The study aims to understand the impact of NO on CAR-T cell persistence and anti-tumor efficacy, and to identify potential solutions to combat NO stress and improve CAR-T therapy outcomes. The methodology used includes in vitro experiments with CAR-T cells and a mouse tumor model, as well as analysis of mitochondrial dynamics and T-cell activation markers. The primary objective of the study is to identify the mechanisms underlying NO-induced impairment of CAR-T cell persistence and functionality, and to develop strategies to enhance CAR-T cell expansion and anti-tumor capacity.

Comparative Analysis & Findings

  • The study found that continuous signaling from CAR promotes excessive NO production, which in turn suppresses S-nitrosoglutathione reductase (GSNOR) expression in T cells. This leads to increased protein S-nitrosylation, resulting in impaired mitochondrial fitness and deficiency of T cell stemness. Enforced expression of GSNOR promotes memory differentiation of CAR-T cells, rendering them better resistance to mitochondrial dysfunction and enhancing their expansion and anti-tumor capacity in vitro and in a mouse tumor model. These findings suggest that NO stress plays a critical role in restricting CAR-T cell persistence and functionality, and that GSNOR overexpression may provide a solution to combat NO stress and improve CAR-T therapy outcomes.

Implications and Future Directions

  • The study's findings have significant implications for the development of CAR-T therapy for refractory or relapsed lymphoma and leukemia patients. The study identifies a critical role of NO in restricting CAR-T cell persistence and functionality, and suggests that GSNOR overexpression may provide a solution to combat NO stress and improve CAR-T therapy outcomes. Future research directions could include further investigation of the mechanisms underlying NO-induced impairment of CAR-T cell persistence and functionality, as well as development of novel strategies to enhance CAR-T cell expansion and anti-tumor capacity in vivo. The study's findings could also have broader implications for the development of other T-cell-based therapies, as NO stress is known to play a role in T-cell activation and function.